Encoded Therapeutics

Encoded Therapeutics Employees

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Encoded Therapeutics Company Information

Encoded Therapeutics is a biotechnology company specializing in the development of precision gene therapies for pediatric central nervous system (CNS) disorders. Their flagship program, ETX101, is aimed at treating Dravet syndrome, a severe developmental and epileptic encephalopathy, by modulating the SCN1A gene in a cell-selective manner. This approach seeks to address the root cause of the syndrome. Encoded Therapeutics is also conducting the ENVISION study, a natural history study to better understand the progression of Dravet syndrome in affected children. The company has received regulatory approvals for ETX101, including UK CTA approval and US IND clearance, positioning it as a promising gene therapy candidate for Dravet syndrome. Beyond ETX101, Encoded Therapeutics is developing a pipeline of potential therapies for other pediatric CNS disorders, as well as treatments for liver, metabolic, and cardiovascular diseases. The company leverages a novel targeting and regulation platform to enhance the specificity and potency of its gene therapies. Encoded Therapeutics is headquartered in South San Francisco, CA, and maintains a research facility in Research Triangle Park, NC.

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